Rare DiseaseChromosomal / Neurodevelopmental

9p Deletion Syndrome (Alfi's Syndrome)

Your 9p patients' hardest days happen between visits, where no scale is watching.

9p deletion syndrome attacks on every front at once, seizures, a dysmotile gut, a feeding tube, slowed development, yet clinic visits see only a thin slice, months apart. The titration that finally calms the seizures, the three stool-free days before a bilious-vomiting crisis, the granulation creeping around the button: all of it unfolds at home. Forma captures that continuous, multi-system reality in the caregiver's own voice.

How it works

15 seconds of speech. 25 data points.

Forma turns each child into a continuous data stream that families can actually sustain. Caregivers speak or type a single sentence in the moment, under a minute, and the platform structures it into typed observations across seizures, medications and CBD titration, GI and feeding symptoms, G-tube care, bowels, development, sleep, and behavior. Distinctive 9p signals are built in: a bowel-obstruction red-flag view and gastric residual volume captured with its color. Everything threads back to existing clinical assessments and a caregiver Global Impression anchor, so neurology, GI, and research teams see the same longitudinal picture.

Patient speaking

😊
Today

Forecast

Based on prior Topics logging

😴
Fatigue
MTWTFSS
🤗
Mood

Topics

💧
Seizure Event
🔥
Medication
💊
Post-ictal
💧
Sleep Quality
🔥
Triggers
0
data points extracted
Research-Ready Dataset

Structured, coded, longitudinal

Timing
Seizure time:6:00 AMSeizure duration:45 secRecovery time:20 minMissed dose time:Previous evening
Location
Injury location:Tongue
Severity
Injury:Tongue bitePost-ictal symptom:Confusion
Actions
Adherence:Missed doseMedication:Keppra
Environmental
Barometric pressure:29.82 inHg (falling)Moon phase:Waxing gibbous (87%)

From data to insights

What the data reveals

Daily voice logs compound into actionable insights, for patients managing their condition and for researchers running studies.

For Patients

Forma Insights

Is the CBD actually helping Leo's seizures?

Yes, his logged seizures dropped from an average of 2.8 per day in week 1 to 0.6 per day by week 3, after two titration steps, including three seizure-free days in the last week.

Avg seizures/day by week

When is Leo most likely to get a blocked-up belly?

All four of his bilious-vomiting episodes in the last six weeks followed three or more days without a bowel movement, and his belly was flagged as hard or distended a day before the ER trip on Day 8.

Obstruction risk by stool-free days

How are his feeds going overall?

Feed intolerance averaged 6 out of 10 during the obstruction week but settled to about 1 out of 10 in the two weeks after, and he tolerated roughly 90% of his prescribed volume once feeds resumed.

Feed intolerance over time

Can you summarize Leo's last few weeks for his doctor?

Over 21 days Leo's seizures fell from ~3/day at baseline to three seizure-free days by week 3, across two Epidiolex titration steps (Days 4 and 13). A Day 8 obstruction (3 stool-free days, distension, bilious vomiting) led to a brief admission and clean-out; feeds and seizures both improved afterward, and on Day 18 he took purees by mouth for the first time.

For Researchers

app.formahealth.io/research/insights
Research Assistant9p Deletion Syndrome (Alfi's Syndrome) Monitoring Cohort

Is off-label cannabidiol reducing seizure burden across the 9p cohort?

Across N=34 children with 9p deletion on off-label cannabidiol, median weekly seizure frequency fell 47% (IQR 28–61%) over 8 weeks of titration, with a significant mixed-effects time slope (p=0.002).

Median seizures/week

Trend

Can caregiver logs predict bowel-obstruction events before they escalate?

A composite of three or more stool-free days plus reported abdominal distension predicted bilious-vomiting/obstruction events with sensitivity 0.82 and specificity 0.76 (AUC 0.81) across N=41 events.

Early-warning sensitivity

Trend

How does cannabidiol tolerability track with titration in real-world use?

Caregiver-reported somnolence clustered within 7 days of each titration step (OR 3.4, 95% CI 1.9–6.1), and elevated-LFT flags in 11% of patients surfaced a mean of 9 days before scheduled lab draws.

Somnolence vs titration day

Trend

Is daily logging sustainable, and does the Global Impression anchor hold up?

Daily voice-log adherence was 78% at 8 weeks (N=52), and the caregiver Global Impression of change correlated with measured seizure reduction (Spearman ρ=0.63, p<0.001), supporting its use as an interim anchor absent a validated 9p PRO.

Adherence by week

Trend

The raw signal

12 days of raw patient data

The day-by-day voice log behind the insights above, and the detail that periodic check-ins can't capture.

Mon, May 4Day 1

Leo had multiple seizures and threw up after his morning feed, a hard start to the week.

Seizures 3Feeding/GI 2
Tue, May 5Day 2

Up four times overnight, restless, and one episode looked like a seizure in his sleep.

Sleep 3Seizures 2
Thu, May 7Day 4
💊Epidiolex titration step (toward 10 mg/kg)

Neurology moved Leo to the next Epidiolex titration step, aiming for 10 mg/kg.

Sat, May 9Day 6
Granulation tissue + site leakage

Granulation tissue came back around the button and the site was leaking again.

G-tube 2
Mon, May 11Day 8
🚨ER, suspected bowel obstruction & dehydration

Three days without a bowel movement, a hard distended belly, and green vomiting, rushed to the ER.

Feeding/GI 3
Tue, May 12Day 9

Admitted overnight; feeds were held and a clean-out was started to clear the obstruction.

Feeding/GI 3
Thu, May 14Day 11

Home and feeding again, and his seizures were already a little less frequent than baseline.

Seizures 2Feeding/GI 1
Sat, May 16Day 13
💊Epidiolex titration step 2

Second Epidiolex titration step now that his gut has settled.

Mon, May 18Day 15

Slept through most of the night with no seizures, the best night in weeks.

Sleep 1Seizures 1
Thu, May 21Day 18

Took three spoons of puree by mouth without gagging, a real feeding-skill win.

Development 1Feeding/GI 1
Sat, May 23Day 20
First seizure-free day

First completely seizure-free day in three weeks.

Seizures 0
Sun, May 24Day 21

Marisol's overall read: Leo is much better than a month ago, especially his seizures and his mood.

Seizures 0Feeding/GI 1

Key insight

Over three weeks, Leo's seizure scores fall from 3 at baseline (Days 1–2) to 0 by Day 20, bracketing two Epidiolex titration steps on Day 4 and Day 13. The arc isn't smooth, a Day 8 emergency (three stool-free days, a hard belly, and bilious vomiting) drives an obstruction admission that a clinic visit would never have caught in time. By Day 18 Leo is taking purees by mouth, the kind of gain that only surfaces when someone logs every day.

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